newsletter-itvisma-ema-chmp-recommends-novartis-smn1-gene-therapy-for-older-sma-patients

News post newsletter-itvisma-ema-chmp-recommends-novartis-smn1-gene-therapy-for-older-sma-patients from the SMA Research Platform — cited research evidence, computational findings and platform updates, loaded live from the database. SMA here means 5q spinal muscular atrophy, the SMN1-linked motor neuron disease — not α-SMA (alpha smooth muscle actin, ACTA2).