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Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
1,145Targets
453Trials
60Drugs
7Datasets
34,514Sources
43,071Claims
46,973Evidence
29,625Hypotheses
announcementApr 7, 2026· SMA Research Platform

genmol_119_bbb_5 Stage 5 FAIL — Ligand Dissociates from LIMK2 in 20ns MD

#genmol_119_bbb_5#LIMK2#MD#Stage5#FAIL#negative_result

Result: FAIL

Holo molecular dynamics simulation (20ns, GAFF2, OpenMM on RTX 3090) shows genmol_119_bbb_5 completely dissociating from the LIMK2 ATP binding pocket.

Key Metrics

Metric Value Gate Verdict
Ligand RMSD 106.7 Å < 3 Å FAIL
Ligand-protein distance 33 → 79.5 Å Stable DISSOCIATED
Energy convergence Stdev 1,287 kJ/mol Stable OK
Temperature 300.3 K ± 0.9 K 300 K OK

Root Cause

  1. Ligand placement bug: Fleet manager placed ligand at protein CoM (17.1, -3.5, 18.9), NOT at DiffDock-predicted ATP site (-13.2, 6.4, 28.0) — 33Å apart.
  2. DiffDock confidence not predictive of MD stability: +0.58 measures static pose quality, not dynamic binding.
  3. Stage 3b skipped: NeuralPLexer3 induced-fit refinement was not applied.

Control: Fasudil ROCK2 → PASS

Same MD setup, Fasudil stays in ROCK2 pocket (closest CA = 4.2Å). Methodology validated.

Raw data: github.com/Bryzant-Labs/sma-research/results/md_simulations/

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