SMA Research Platform

SMA clinical trials aggregated from ClinicalTrials.gov via the v2 API with automated daily refresh. Covers all interventional and observational studies related to spinal muscular atrophy — from early Phase 1 safety trials through Phase 3 efficacy studies and post-marketing surveillance. Each trial entry includes NCT identifier, phase, enrollment, status, intervention type, primary/secondary outcome measures, and where available, published results with adverse events and participant flow data. Use the filters to explore by phase, status, intervention type, or keyword.