SMA Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
14,766Targets
453Trials
84Drugs
7Datasets
6,987Sources
64,683Claims
72,052Evidence
29,649Hypotheses
TARGETproteinHomo sapiens

STMN1

Linked hypotheses (20)

  • risperidone × STMN1 affinity via computational screening (Boltz-2)
    repurposingconf 91%
  • risperidone binds STMN1 (Boltz-2 iPTM=0.906)
    targetconf 91%
  • risperidone binds STMN1 (Boltz-2 iPTM=0.911)
    targetconf 91%
  • aspirin × STMN1 affinity via computational screening (Boltz-2)
    mechanismconf 90%
  • aspirin binds STMN1 (Boltz-2 iPTM=0.904)
    targetconf 90%
  • riluzole × STMN1 affinity via computational screening (Boltz-2)
    repurposingconf 89%
  • riluzole binds STMN1 (Boltz-2 iPTM=0.890)
    targetconf 89%
  • risperidone binds STMN1 (Boltz-2 iPTM=0.887)
    targetconf 89%
  • Y27632 × STMN1 affinity via computational screening (Boltz-2)
    mechanismconf 88%
  • Y27632 binds STMN1 (Boltz-2 iPTM=0.879)
    targetconf 88%
  • risperidone binds STMN1 (Boltz-2 iPTM=0.866)
    targetconf 87%
  • ROCK2 × STMN1 interaction (auto-validated BOLTZ2_PPI iPTM=0.87)
    mechanismconf 87%
  • riluzole binds STMN1 (Boltz-2 iPTM=0.859)
    targetconf 86%
  • risperidone × STMN1 affinity via computational screening (Boltz-2)
    repurposingconf 85%
  • risperidone binds STMN1 (Boltz-2 iPTM=0.846)
    targetconf 85%
  • NRG1 × STMN1 interaction (auto-validated BOLTZ2_PPI iPTM=0.85)
    regeneration_axonconf 85%
  • SMN1 × STMN1 interaction (auto-validated BOLTZ2_PPI iPTM=0.85)
    mechanismconf 85%
  • LIMKi3 binds STMN1 (Boltz-2 iPTM=0.841)
    targetconf 84%
  • LIMKi3 binds STMN1 (Boltz-2 iPTM=0.837)
    targetconf 84%
  • LIMKi3 × STMN1 affinity via computational screening (Boltz-2)
    mechanismconf 84%

Top compound hits (10)

Compound IDSMILESScoreTier
simon_tier2_r436_ac922a585bCOc1ccc(-c2cc(=O)c3c(O)cc(O)cc3o2)cc11.356early
simon_tier2_r226_1903ec3580Cc1nc(-c2ccc(F)cc2)c(-c2ccnc(NC(=O)C3CC3)c2)[nH]11.356early
simon_tier2_r201_6caff24982CCn1c(-c2nonc2N)nc2cnc(OC)cc211.309early
simon_tier2_r98_a220e9fcffCOCCNc1cc(C)nc(-c2ccc(Br)cc2)n11.245early
simon_tier2_r471_f37f937bddCc1cc(Oc2cncc(F)c2)cc(C(=O)Nc2ccc(Cl)cn2)n11.217early
simon_tier2_r362_6728a14394CN(Cc1ccccc1)C(=O)Nc1nc(-c2ccncc2)cs11.185early
simon_tier2_r421_7fb217e0dfCOc1cccc([C@@H](C)NC(=O)Nc2nc(-c3ccncc3)cs2)c11.181early
simon_tier2_r457_f3fecc7932COc1cc(CNC(=O)c2ccc(-c3cn[nH]c3)c(OC)c2)ccc1F1.122early
simon_tier2_r190_05ed4f8a95COc1cc(C(=O)N[C@H](C)c2ccccc2)ccc1-c1cn[nH]c11.087early
simon_tier2_r97_858dbdd9eaC[C@@H](N)[C@H]1CC[C@H](C(=O)Nc2ccncc2)CC11.082early

Linked claims (50)

TypePredicateConfSource
drug targetboltz2_iptm91%
drug targetboltz2_iptm91%
drug targetboltz2_iptm90%
drug targetboltz2_iptm89%
drug targetboltz2_iptm89%
drug targetboltz2_iptm88%
drug targetboltz2_iptm87%
drug targetboltz2_iptm86%
drug targetboltz2_iptm85%
drug targetboltz2_iptm84%
drug targetboltz2_iptm84%
drug targetboltz2_iptm83%
drug targetboltz2_iptm83%
drug targetboltz2_iptm81%
drug targetboltz2_iptm81%
drug targetboltz2_iptm81%
drug targetboltz2_iptm81%
drug targetboltz2_iptm80%
drug targetboltz2_iptm79%
drug targetboltz2_iptm79%

Showing 20 of 50.

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