SMA Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
14,766Targets
453Trials
84Drugs
7Datasets
6,987Sources
64,683Claims
72,052Evidence
29,649Hypotheses
TARGETproteinHomo sapiens

PFN2Profilin-2

Description

Brain-enriched profilin. 7.6x enriched in motor neurons (GSE287257). Actin monomer binding and recycling.

Linked hypotheses (20)

  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%
  • [Biomarker] PFN2 is implicated in SMA pathogenesis based on 6 converging claims
    targetconf 88%

Top compound hits (10)

Compound IDSMILESScoreTier
TUDCAC[C@H]([C@H]1CC[C@H]2[C@@H]1[C@H](O)C[C@@H]1[C@@]2(C)CC[C@H]...0.153promising
LIMKi3Nc1nccc(-c2[nH]nc3CCCCc23)n10.095promising
SCH_772984CN1CCN(C(=O)c2ccc(F)cn2)CC10.050promising
COc1ccc(C(=O)Nc2ccc(COc1ccc(C(=O)Nc2ccc(Br)cn2)cc10.948early
COc1ccc(C(=O)Nc2cc(BCOc1ccc(C(=O)Nc2cc(Br)ccn2)cc10.948early
Cc1ccc(C(=O)NCc2ccc(Cc1ccc(C(=O)NCc2ccc(-c3ccccc3)nc2)cc10.947early
Cc1ccnc(CNC(=O)c2cccCc1ccnc(CNC(=O)c2ccc(F)cc2Br)c10.947early
Cc1cccc(CNC(=O)c2cccCc1cccc(CNC(=O)c2ccc(Br)cn2)n10.947early
N#Cc1ccnc(CNC(=O)c2cN#Cc1ccnc(CNC(=O)c2ccc(Br)cc2)c10.947early
O=C1CC(c2ccc(O)cc2)=O=C1CC(c2ccc(O)cc2)=NN1Cc1ccc(Cl)cc10.946early

Linked claims (50)

TypePredicateConfSource
drug targetboltz2_iptm88%
drug targetboltz2_iptm87%
protein interactionboltz2_ppi_iptm86%
drug targetboltz2_iptm86%
protein interactionboltz2_ppi_iptm86%
drug targetboltz2_iptm85%
drug targetboltz2_iptm83%
drug targetboltz2_iptm83%
drug targetboltz2_iptm82%
drug targetboltz2_iptm82%
protein interactionboltz2_ppi_iptm81%
protein interactionboltz2_ppi_iptm81%
drug targetboltz2_iptm81%
drug targetboltz2_iptm80%
drug targetboltz2_iptm79%
drug targetboltz2_iptm79%
drug targetboltz2_iptm78%
drug targetboltz2_iptm78%
drug targetboltz2_iptm78%
drug targetboltz2_iptm77%

Showing 20 of 50.

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