SMA Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
14,766Targets
453Trials
84Drugs
7Datasets
6,987Sources
64,683Claims
72,052Evidence
29,649Hypotheses
DRUGapprovedsplice modifier

risdiplam tablet

Brand names: Evrysdi tablet

Mechanism

Tablet formulation of risdiplam (Evrysdi). SMN2 splicing modifier for improved oral bioavailability.. Tablet formulation FDA-approved May 2024 (Genentech/Roche) for SMA patients ≥2 years and ≥20 kg.

Approved indications

SMA (tablet, ≥2y ≥20kg)

Related claims (0)

No claims matched “risdiplam tablet” in free-text search.

Off-Target Findings (0)

No Boltz-2 / Chai-1 off-target panel claims recorded for this drug.

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