DRUGapprovedsplice modifier
risdiplam tablet
Brand names: Evrysdi tablet
Mechanism
Tablet formulation of risdiplam (Evrysdi). SMN2 splicing modifier for improved oral bioavailability.. Tablet formulation FDA-approved May 2024 (Genentech/Roche) for SMA patients ≥2 years and ≥20 kg.
Approved indications
SMA (tablet, ≥2y ≥20kg)
Related claims (0)
No claims matched “risdiplam tablet” in free-text search.
Off-Target Findings (0)
No Boltz-2 / Chai-1 off-target panel claims recorded for this drug.