SMA Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
15,945Targets
453Trials
85Drugs
7Datasets
8,004Sources
221,721Claims
232,882Evidence
73,172Hypotheses
DRUGapprovedsplice modifier

risdiplam tablet

Brand names: Evrysdi tablet

Mechanism

Tablet formulation of risdiplam (Evrysdi). SMN2 splicing modifier for improved oral bioavailability.. Tablet formulation FDA-approved May 2024 (Genentech/Roche) for SMA patients ≥2 years and ≥20 kg.

Approved indications

SMA (tablet, ≥2y ≥20kg)

Related claims (0)

No claims matched “risdiplam tablet” in free-text search.

Off-Target Findings (0)

No Boltz-2 / Chai-1 off-target panel claims recorded for this drug.

Login → Command Center