SMA Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
14,766Targets
453Trials
84Drugs
7Datasets
6,987Sources
64,683Claims
72,052Evidence
29,649Hypotheses
DRUGphase2small molecule

reldesemtiv

Mechanism

Fast skeletal muscle troponin activator. Enhances muscle force production.

Related claims (9)

TypePredicateConfSource
protein interactionReldesemtiv binding interactions with troponin include conventional hydrogen bonds, carbon hydrogen bonds, pi-alkyl, pi-sulfur and halogen interactions.59%36959428
protein interactionReldesemtiv binding to the fast skeletal troponin complex induces conformational compacting of troponin C characterized by reduced solvent exposure.59%36959428
protein interactionReldesemtiv binding to troponin C sensitizes the protein to calcium through conformational changes that favor slow calcium ion release.53%36959428
protein interactionArg113, Met116, Val114, and Met121 in the switch region of the inhibitory troponin subunit are critical residues for Reldesemtiv binding and contribute substantially to binding free energy.53%36959428
drug efficacyReldesemtiv is proposed as a potential treatment for neurogenic neuromuscular diseases including spinal muscular atrophy by increasing muscle strength through troponin activation.53%36959428
drug targetReldesemtiv is a second-generation small molecule developed to activate fast skeletal muscle troponin complex with improved specificity and reduced off-target effects.53%36959428
drug efficacyThe change from baseline in 6MWD was greater for reldesemtiv 450 mg than for placebo at weeks 4 and 8 (clinical trial result).51%33624184
drug efficacyChanges from baseline in MEP at week 8 on reldesemtiv 150 and 450 mg were significantly greater than those on placebo (clinical trial result).51%33624184
drug efficacyResults suggest reldesemtiv may offer clinical benefit (clinical trial result).45%33624184

Off-Target Findings (0)

No Boltz-2 / Chai-1 off-target panel claims recorded for this drug.

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