SMA Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
14,766Targets
453Trials
84Drugs
7Datasets
6,987Sources
64,683Claims
72,052Evidence
29,649Hypotheses
DRUGpreclinicalsmall molecule

chembl1528069

Mechanism

pyrazol-1-yl-aminopyrimidine; SMN1/SMN2 binder pchembl=8.55, BBB=0.90

Structure

Cc1cc(-n2nc(C)cc2C)nc(N)n1

Related claims (0)

No claims matched “chembl1528069” in free-text search.

Off-Target Findings (0)

No Boltz-2 / Chai-1 off-target panel claims recorded for this drug.

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