SMA Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
15,945Targets
453Trials
85Drugs
7Datasets
8,004Sources
221,721Claims
232,882Evidence
73,172Hypotheses
DRUGpreclinicalsmall molecule

chembl1528069

Mechanism

pyrazol-1-yl-aminopyrimidine; SMN1/SMN2 binder pchembl=8.55, BBB=0.90

Structure

Cc1cc(-n2nc(C)cc2C)nc(N)n1

Related claims (0)

No claims matched “chembl1528069” in free-text search.

Off-Target Findings (0)

No Boltz-2 / Chai-1 off-target panel claims recorded for this drug.

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