SMA Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
13,282Targets
453Trials
84Drugs
7Datasets
42,694Sources
48,101Claims
55,096Evidence
29,646Hypotheses
DRUGpreclinicalsmall molecule

chembl1483828

Mechanism

methoxybenzene sulfonamide; SMN1/SMN2 binder pchembl=8.80, BBB=0.74

Structure

COc1ccc(S(=O)(=O)N(C)CC(=O)N2CCC(C(N)=O)CC2)cc1

Related claims (0)

No claims matched “chembl1483828” in free-text search.

Off-Target Findings (0)

No Boltz-2 / Chai-1 off-target panel claims recorded for this drug.

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