DRUGapprovedsmall molecule
arimoclomol
Brand names: Miplyffa
Mechanism
Hydroxylamine HSP70/HSP90 co-inducer. Preserves NMJ structure in SOD1-G93A ALS mice (PMID 22591194). Approved for Niemann-Pick type C (2024). Candidate SMA adjunct.
Approved indications
niemann-pick-c
Related claims (0)
No claims matched “arimoclomol” in free-text search.
Off-Target Findings (0)
No Boltz-2 / Chai-1 off-target panel claims recorded for this drug.