SMA Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
13,058Targets
453Trials
84Drugs
7Datasets
42,617Sources
48,024Claims
55,019Evidence
29,646Hypotheses

Molecular Docking

COMPUTATIONAL
9 scored · 8 strong · 1 moderate

Pharmacophore-based docking score prediction for SMA drug candidates against SMN2 target binding pockets. Scores compounds by shape complementarity, H-bond potential, hydrophobic match, electrostatic alignment, and strain penalty.

How does docking scoring work?

Docking scores predict how well a small molecule fits into a protein binding pocket. Higher composite scores indicate better predicted binding. Binding class: strong (composite ≥ 0.7, high-confidence), moderate (0.4–0.7, worth investigating), weak(< 0.4).

Sub-scores. Shape — geometric fit. H-Bond— donor/acceptor complementarity. Hydrophobic — contact area. Electrostatic — charge complementarity. Strain— penalty for unfavorable ligand conformation (lower is better). Benchmark: riluzole scores +0.082 against its best target.

Data source:sma-research/docking/— diffdock_results.json, vina_scores.json, per-campaign pocket folders
9
Compounds Scored
8
Strong Binders
1
Moderate Binders
CHEMBL305177
Top Hit
5' splice site / U1 snRNP interface
Binding Pocket
Pocket
5' splice site / U1 snRNP interface \u2014 SMN2
Volume 380 \u00c5\u00b3 \u00b7 Polar contacts 10 \u00b7 MW 200\u2013500 \u00b7 logP -0.5\u20132.5
Risdiplam binding site — small molecule stabilizes U1 snRNP at exon 7 5'ss. Requires flat, aromatic compounds with H-bond donors.
Ref: Modeled from risdiplam-SMN2 (Sivaramakrishnan, Nat Chem Biol 2023)
Min score0.00
9 / 9 rows

Top Predicted Binders

#CompoundTargetAffinity (kcal/mol)ShapeH-BondHydrophobicScoreClass3D
1CHEMBL305177MTOR_PATHWAY-121.000.701.001.00strong
2CHEMBL369258MTOR_PATHWAY-11.61.000.400.930.96strong
3CHEMBL170760MTOR_PATHWAY-11.61.000.400.870.94strong
4CHEMBL171765MTOR_PATHWAY-11.31.000.600.510.91strong
5CHEMBL38735MTOR_PATHWAY-11.11.000.600.430.89strong
6CHEMBL35364MTOR_PATHWAY-10.90.980.901.000.87strong
7CHEMBL410215MTOR_PATHWAY-10.31.000.800.620.78strong
8CHEMBL344018MTOR_PATHWAY-9.81.000.800.350.73strong
9CHEMBL250213MTOR_PATHWAY-9.41.000.800.050.67moderate
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